
eBook - PDF
Duchenne Muscular Dystrophy
Advances in Therapeutics
- 496 pages
- English
- PDF
- Available on iOS & Android
eBook - PDF
Duchenne Muscular Dystrophy
Advances in Therapeutics
About this book
Duchenne Muscular Dystrophy (DMD) is one of the most prevalent genetic disorders of childhood and currently stands as an incurable condition. This authoritative guide provides a clear overview of the latest current and experimental approaches to the treatment of DMD and examines the clinical, genetic, and pathophysiological aspects of the disease i
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Yes, you can access Duchenne Muscular Dystrophy by Jeffrey S. Chamberlain, Thomas A. Rando, Jeffrey S. Chamberlain,Thomas A. Rando in PDF and/or ePUB format, as well as other popular books in Medicine & Genetics in Medicine. We have over one million books available in our catalogue for you to explore.
Information
Table of contents
- Front Cover
- Preface
- Contents
- Introduction
- 1. Clinical Overview of Duchenne Muscular Dystrophy
- 2. The Functional Biology of Dystrophin: Structural Components and the Pathogenesis of Duchenne Muscular Dystrophy
- 3. The Functional Biology of Dystrophin: Associated Signaling Pathways and Potential Targets for Therapeutic Intervention
- 4. Duchenne Muscular Dystrophy and Becker Muscular Dystrophy: Diagnostic Principles
- 5. Mutation Detection
- 6. Protein Studies in Duchenne Muscular Dystrophy
- 7. Medical Management of Duchenne Muscular Dystrophy
- 8. Rehabilitation Management of Duchenne Muscular Dystrophy
- 9. Orthopedic Interventions in the Management of Duchenne Muscular Dystrophy
- 10. Therapeutic Principles and Challenges in Duchenne Muscular Dystrophy
- 11. Experimental Pharmacologic Therapies in Duchenne Dystrophy: Current Clinical Trials
- 12. Utrophin: The Intersection Between Pharmacological and Genetic Therapy
- 13. Regenerative Therapy
- 14. Cellular Mediated Delivery: The Intersection Between Regenerative Medicine and Genetic Therapy
- 15. Oligonucleotide-Mediated Exon Skipping and Gene Editing for Duchenne Muscular Dystrophy
- 16. The Intravascular Delivery of Naked DNA for Treating Duchenne Muscular Dystrophy
- 17. Adenoviral-Mediated Gene Therapy
- 18. Retroviridae-Based Gene Transfer Vectors in Duchenne Muscular Dystrophy Therapy
- 19. Gene Therapy of Muscular Dystrophy Using Adeno-Associated Viral Vectors: Promises and Limitations
- 20. Regional and Systemic Gene Delivery Using Viral Vectors
- Index
- Back Cover