Duchenne Muscular Dystrophy (DMD) is one of the most prevalent genetic disorders of childhood and currently stands as an incurable condition. This authoritative guide provides a clear overview of the latest current and experimental approaches to the treatment of DMD and examines the clinical, genetic, and pathophysiological aspects of the disease i

eBook - PDF
Duchenne Muscular Dystrophy
Advances in Therapeutics
- 491 pages
- English
- PDF
- Available on iOS & Android
eBook - PDF
Duchenne Muscular Dystrophy
Advances in Therapeutics
About this book
Trusted by 375,005 students
Access to over 1.5 million titles for a fair monthly price.
Study more efficiently using our study tools.
Information
Topic
MedicineSubtopic
Genetics in MedicineTable of contents
- Front Cover
- Preface
- Contents
- Introduction
- 1. Clinical Overview of Duchenne Muscular Dystrophy
- 2. The Functional Biology of Dystrophin: Structural Components and the Pathogenesis of Duchenne Muscular Dystrophy
- 3. The Functional Biology of Dystrophin: Associated Signaling Pathways and Potential Targets for Therapeutic Intervention
- 4. Duchenne Muscular Dystrophy and Becker Muscular Dystrophy: Diagnostic Principles
- 5. Mutation Detection
- 6. Protein Studies in Duchenne Muscular Dystrophy
- 7. Medical Management of Duchenne Muscular Dystrophy
- 8. Rehabilitation Management of Duchenne Muscular Dystrophy
- 9. Orthopedic Interventions in the Management of Duchenne Muscular Dystrophy
- 10. Therapeutic Principles and Challenges in Duchenne Muscular Dystrophy
- 11. Experimental Pharmacologic Therapies in Duchenne Dystrophy: Current Clinical Trials
- 12. Utrophin: The Intersection Between Pharmacological and Genetic Therapy
- 13. Regenerative Therapy
- 14. Cellular Mediated Delivery: The Intersection Between Regenerative Medicine and Genetic Therapy
- 15. Oligonucleotide-Mediated Exon Skipping and Gene Editing for Duchenne Muscular Dystrophy
- 16. The Intravascular Delivery of Naked DNA for Treating Duchenne Muscular Dystrophy
- 17. Adenoviral-Mediated Gene Therapy
- 18. Retroviridae-Based Gene Transfer Vectors in Duchenne Muscular Dystrophy Therapy
- 19. Gene Therapy of Muscular Dystrophy Using Adeno-Associated Viral Vectors: Promises and Limitations
- 20. Regional and Systemic Gene Delivery Using Viral Vectors
- Index
- Back Cover
Frequently asked questions
Yes, you can cancel anytime from the Subscription tab in your account settings on the Perlego website. Your subscription will stay active until the end of your current billing period. Learn how to cancel your subscription
No, books cannot be downloaded as external files, such as PDFs, for use outside of Perlego. However, you can download books within the Perlego app for offline reading on mobile or tablet. Learn how to download books offline
Perlego offers two plans: Essential and Complete
- Essential is ideal for learners and professionals who enjoy exploring a wide range of subjects. Access the Essential Library with 800,000+ trusted titles and best-sellers across business, personal growth, and the humanities. Includes unlimited reading time and Standard Read Aloud voice.
- Complete: Perfect for advanced learners and researchers needing full, unrestricted access. Unlock 1.5M+ books across hundreds of subjects, including academic and specialized titles. The Complete Plan also includes advanced features like Premium Read Aloud and Research Assistant.
We are an online textbook subscription service, where you can get access to an entire online library for less than the price of a single book per month. With over 1.5 million books across 990+ topics, we’ve got you covered! Learn about our mission
Look out for the read-aloud symbol on your next book to see if you can listen to it. The read-aloud tool reads text aloud for you, highlighting the text as it is being read. You can pause it, speed it up and slow it down. Learn more about Read Aloud
Yes! You can use the Perlego app on both iOS and Android devices to read anytime, anywhere — even offline. Perfect for commutes or when you’re on the go.
Please note we cannot support devices running on iOS 13 and Android 7 or earlier. Learn more about using the app
Please note we cannot support devices running on iOS 13 and Android 7 or earlier. Learn more about using the app
Yes, you can access Duchenne Muscular Dystrophy by Jeffrey S. Chamberlain, Thomas A. Rando, Jeffrey S. Chamberlain,Thomas A. Rando in PDF and/or ePUB format, as well as other popular books in Medicine & Genetics in Medicine. We have over 1.5 million books available in our catalogue for you to explore.