In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders
eBook - PDF

In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders

  1. 198 pages
  2. English
  3. PDF
  4. Available on iOS & Android
eBook - PDF

In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders

About this book

Ongoing advances in pharmaceutical biotechnology have paved the way to ground-breaking new biological therapeutic modalities, offering the possibility of a durable curative approach for a number of life-threatening diseases, for which the medical need is as yet unmet. Over the past decades, gene therapy has seen a massive transformation from a proof-of-concept approach to a clinical reality culminating in the regulatory approval of state-of-the-art products in the European Union and in the United States. This book captures some of the scientific progresses notably in gene transfer technologies and translational development of in vivo and ex vivo gene therapy interventions in the treatment of a broad range of complex and debilitating non-inherited and inherited disorders such as: human immunodeficiency virus 1 (HIV-1) infection, cancer, cystic fibrosis, hereditary retinopathies, haemophilia B, cardiac diseases, and chronic liver fibrosis.

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Yes, you can access In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders by Houria Bachtarzi in PDF and/or ePUB format, as well as other popular books in Medicine & Genetics in Medicine. We have over one million books available in our catalogue for you to explore.

Information

Publisher
IntechOpen
Year
2019
Print ISBN
9781789857177
eBook ISBN
9781839620829
Topic
Medicine
Subtopic
Genetics in Medicine

Table of contents

  1. In Vivo and Ex Vivo Gene Therapy for Inherited and Non-Inherited Disorders
  2. Preface
  3. Contents
  4. Section 1 Gene Transfer Technologies for In Vivo and Ex Vivo Applications
  5. Section 2 Advances in Virotherapy: Virus-based Gene Therapy for Cancer and Other Genetic Diseases
  6. Section 3 Cardiac Gene Therapy